Breathing Hope: Advancements in Pediatric Cystic Fibrosis Care
Life has changed for children – and the increasing number of adults – with CF, thanks to new mutation-specific therapies. Pediatric pulmonologist Elizabeth Gibb, MD, MPhil, reviews the genetics of CF, notes shortcomings of the newborn screening process (which differs by state), and explains how CFTR modulators work to improve respiratory and digestive function – as well as which patients aren’t eligible for the drugs and why. Learn how providers can help address ethnic disparities in care and hear about exciting treatments on the horizon, such as inhaled mRNA therapy.
Learning Objectives:
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List the diverse ways in which patients with cystic fibrosis present.
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Explain the mechanism of Cystic Fibrosis transmembrane Conductance Regulator (CFTR) modulator therapy.
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Describe future directions in the treatment of cystic fibrosis, especially as it pertains to genetic therapy.
Accreditation Statement
UCSF Benioff Children’s Hospital Oakland is accredited by the California Medical Association to provide continuing medical education for physicians.
UCSF Benioff Children’s Hospital Oakland designates this recorded activity for a maximum of 1 AMA PRA Category 1 Credit™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.
Disclosures:
No one involved in the planning or presentation of this activity has any relevant financial relationships with a commercial interest to disclose.
Published
August 8, 2025
Expires
August 8, 2026
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